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<a class="text-decoration-none" href="/posts/7410212-embracing-the-imaginative-spirit-of-halloween-sma-news-today-forums"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
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<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Embracing The Imaginative Spirit of Halloween &amp; SMA News Today Forums
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6m
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<span><span class="js-time" data-epochtime="1572393600" data-format="short_date">Oct 30, 2019</span></span>
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<a class="text-decoration-none" href="/posts/7407803-skye-the-first-baby-treated-with-zolgensma-is-getting-stronger-embracing-halloween"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Skye, The First Baby Treated With Zolgensma, Is Getting Stronger &amp; Embracing Halloween
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
6m
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<span><span class="js-time" data-epochtime="1572220800" data-format="short_date">Oct 28, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
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6m
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<a class="text-decoration-none" href="/posts/7406202-oklahoma-ranks-the-lowest-on-programs-that-are-key-to-rare-diseases-recent-columns"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Oklahoma Ranks The Lowest On Programs That Are Key To Rare Diseases &amp; Recent Columns
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
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<span><span class="js-time" data-epochtime="1571961600" data-format="short_date">Oct 25, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
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<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7404078-sma-news-and-perspectives-10-23-19"><div class="Episode-list-grid card-body pan">
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<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
SMA News And Perspectives 10 - 23 - 19
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
6m
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<span class="d-sm-none">
&bull;
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<span><span class="js-time" data-epochtime="1571788800" data-format="short_date">Oct 23, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
6m
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<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7401719-rare-disease-groups-seeking-public-support-to-renew-newborn-screening-act-winter-hibernation"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Rare Disease Groups Seeking Public Support To Renew Newborn Screening Act &amp; Winter Hibernation
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
6m
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<span><span class="js-time" data-epochtime="1571616000" data-format="short_date">Oct 21, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
6m
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<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7400079-baby-girl-s-family-brought-from-the-uk-to-ohio-for-zolgensma-treatment-maid-of-honor"><div class="Episode-list-grid card-body pan">
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<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Baby Girl&#39;s Family Brought From The UK to Ohio For Zolgensma Treatment &amp; Maid of Honor
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
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<span><span class="js-time" data-epochtime="1571356800" data-format="short_date">Oct 18, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
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<a class="text-decoration-none" href="/posts/7397844-overview-of-the-sma-forums-and-recent-discussions-coming-of-age-stories-and-living-with-sma"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Overview Of The SMA Forums And Recent Discussions &amp; Coming-Of-Age Stories And Living With SMA
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
6m
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<span class="d-sm-none">
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<span><span class="js-time" data-epochtime="1571184000" data-format="short_date">Oct 16, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
6m
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7396728-44-roundtable-discussion-discussion-for-october-2019"><div class="Episode-list-grid card-body pan">
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<img srcset="https://audioboom.com/i/35543364/75x75/c 75w, https://audioboom.com/i/35543364/150x150/c 150w, https://audioboom.com/i/35543364/300x300/c 300w, https://audioboom.com/i/35543364/600x600/c 600w, https://audioboom.com/i/35543364/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #352d28; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35543364/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
#44 - Roundtable Discussion - Discussion for October 2019
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Hosts Kevin Schaefer and Michael Morale discuss the latest news regarding SMA therapies Spinraza and Risdiplam, as well as some of our recent columns. Listen here, and share your thoughts in the SMA News Today forums.
For information regarding the DEVOTE trial, please click on the following link:
https://www.clinicaltrials.gov/ct2/show/NCT04089566?term=NCT04089566&amp;rank=1
Are you interested in l...
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
28m
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<span><span class="js-time" data-epochtime="1571097600" data-format="short_date">Oct 15, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
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<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7395185-teen-with-epilepsy-described-as-rare-case-of-sma-alternative-options-for-seating"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Teen With Epilepsy Described As Rare Case of SMA &amp; Alternative Options For Seating
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
7m
</span>
<span class="d-sm-none">
&bull;
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<span><span class="js-time" data-epochtime="1571011200" data-format="short_date">Oct 14, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
7m
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7393432-additional-space-for-zolgensma-production-with-avexis-catalent-partnership-trending-topics"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Additional Space For Zolgensma Production With AveXis Catalent Partnership &amp; Trending Topics
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
4m
</span>
<span class="d-sm-none">
&bull;
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<span><span class="js-time" data-epochtime="1570752000" data-format="short_date">Oct 11, 2019</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
4m
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7391142-problems-with-metabolising-fat-molecules-are-worrisome-in-sma-children-being-inspirational"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Problems With Metabolising Fat Molecules Are Worrisome In SMA Children &amp; Being Inspirational
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
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<span><span class="js-time" data-epochtime="1570579200" data-format="short_date">Oct 09, 2019</span></span>
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</div>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7389357-risdiplam-is-raising-smn-levels-in-older-patients-in-durable-ways-dealing-with-disappointment"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Risdiplam Is Raising SMN Levels In Older Patients In Durable Ways &amp; Dealing With Disappointment
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
</span>
<span class="d-sm-none">
&bull;
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<span><span class="js-time" data-epochtime="1570406400" data-format="short_date">Oct 07, 2019</span></span>
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<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
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<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7387315-adding-reldesemtiv-to-spinraza-improved-muscle-function-in-an-sma-mouse-model-finding-humor"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Adding Reldesemtiv to Spinraza Improved Muscle Function In An SMA Mouse Model &amp; Finding Humor
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1570147200" data-format="short_date">Oct 04, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7385290-prenatal-blood-test-for-sma-is-now-available-rolling-through-the-seasons"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Prenatal Blood Test For SMA Is Now Available &amp; &quot;Rolling Through The Seasons&quot;
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1569974400" data-format="short_date">Oct 02, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7384447-43-interview-with-jeff-olander"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35478233/75x75/c 75w, https://audioboom.com/i/35478233/150x150/c 150w, https://audioboom.com/i/35478233/300x300/c 300w, https://audioboom.com/i/35478233/600x600/c 600w, https://audioboom.com/i/35478233/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #a56d69; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35478233/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
#43 - Interview With Jeff Olander
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
50m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1569888000" data-format="short_date">Oct 01, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
50m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7382986-macedonian-gaucher-activist-for-rare-disease-patients-getting-ready-for-the-cold"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Macedonian Gaucher Activist For Rare Disease Patients &amp; Getting Ready For The Cold
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1569801600" data-format="short_date">Sep 30, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7381185-european-spinraza-label-updated-to-reflect-long-term-benefits-trending-topics"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
European Spinraza Label Updated to Reflect Long-Term Benefits &amp; Trending Topics
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
7m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1569542400" data-format="short_date">Sep 27, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
7m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7378936-high-chance-of-scoliosis-surgery-in-types-1c-and-2-superheroes-with-disabilities"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
High Chance Of Scoliosis Surgery in Types 1C and 2 &amp; Superheroes With Disabilities
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1569369600" data-format="short_date">Sep 25, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7376654-spinraza-gives-babies-with-type-1-sma-hope-for-a-healthy-life-in-north-macedonia"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Spinraza Gives Babies With Type 1 SMA Hope For a Healthy Life in North Macedonia
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
7m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1569196800" data-format="short_date">Sep 23, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
7m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7374575-phase-2-trial-shows-presymptomatic-spinraza-treatment-to-sma-children-reaching-milestones"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Phase 2 Trial Shows Presymptomatic Spinraza Treatment to SMA Children Reaching Milestones
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
7m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1568937600" data-format="short_date">Sep 20, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
7m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7372488-the-world-s-first-alport-stamp-is-a-macedonian-mom-s-latest-win-for-rare-disease-patients"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
The World’s First Alport Stamp is a Macedonian Mom’s Latest Win for Rare Disease Patients
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1568764800" data-format="short_date">Sep 18, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7371142-42-interview-with-kyle-harris"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35409116/75x75/c 75w, https://audioboom.com/i/35409116/150x150/c 150w, https://audioboom.com/i/35409116/300x300/c 300w, https://audioboom.com/i/35409116/600x600/c 600w, https://audioboom.com/i/35409116/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #353535; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35409116/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
#42 - Interview With Kyle Harris
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
36m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1568678400" data-format="short_date">Sep 17, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
36m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7370236-rna-therapy-delivered-by-viral-vector-may-hold-potential-to-treat-sma"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
RNA Therapy Delivered by Viral Vector May Hold Potential to Treat SMA
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1568643926" data-format="short_date">Sep 16, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7368285-why-screening-tests-for-zolgernsma-s-use-are-necessary-motivational-post"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
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</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1568371369" data-format="short_date">Sep 13, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
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<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
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</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1568160000" data-format="short_date">Sep 11, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7362773-study-says-children-with-sma-are-at-risk-of-weak-bones-and-fractures-more-independence"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Study Says Children With SMA Are at Risk of Weak Bones And Fractures &amp; More Independence
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1567987200" data-format="short_date">Sep 09, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7361239-how-avexis-onegene-program-could-help-families-wanting-zolgensma-trending-topics"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
How AveXis’ OneGene Program Could Help Families Wanting Zolgensma &amp; Trending Topics
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1567728000" data-format="short_date">Sep 06, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7359153-future-work-into-zolgensma-gene-therapy-and-other-sma-treatments-physical-books"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Future Work Into Zolgensma, Gene Therapy And Other SMA Treatments &amp; Physical Books
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
13m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1567555200" data-format="short_date">Sep 04, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
13m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7358081-41-roundtable-discussion-discussion-for-september-2019"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35341596/75x75/c 75w, https://audioboom.com/i/35341596/150x150/c 150w, https://audioboom.com/i/35341596/300x300/c 300w, https://audioboom.com/i/35341596/600x600/c 600w, https://audioboom.com/i/35341596/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #d5cebe; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35341596/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
#41 - Roundtable Discussion - Discussion for September 2019
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
31m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1567468800" data-format="short_date">Sep 03, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
31m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7357194-nord-honors-industry-in-patient-advocates-at-rare-impact-awards-gala-overprotective-parents"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
NORD Honors Industry In Patient Advocates At Rare Impact Awards Gala &amp; Overprotective Parents
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1567382400" data-format="short_date">Sep 02, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7355473-anti-epileptic-keppra-can-be-a-candidate-for-sma-treatment-batcave-for-personal-space"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Anti-Epileptic Keppra Can Be A Candidate For SMA Treatment &amp; Batcave For Personal Space
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1567123200" data-format="short_date">Aug 30, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7353491-zolgensma-s-arrival-adds-urgency-to-sma-newborn-screening-efforts-natalie-russo-and-her-brother"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Zolgensma’s Arrival Adds Urgency to SMA Newborn Screening Efforts &amp; Natalie Russo And Her Brother
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1566950400" data-format="short_date">Aug 28, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7351487-eurordis-integrated-care-initiative-for-rare-disease-patients-cooperate-with-physical-therapists"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Eurordis&#39; Integrated Care Initiative For Rare Disease Patients &amp; Cooperate With Physical Therapists
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1566777600" data-format="short_date">Aug 26, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7349982-rna-molecule-mir-23a-may-have-therapeutic-role-in-sma-from-college-writing-course-to-a-career"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
RNA Molecule miR-23a May Have Therapeutic Role in SMA &amp; From College Writing Course To A Career
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1566518400" data-format="short_date">Aug 23, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7347797-zolgensma-s-price-and-its-cure-one-cure-many-potential-concerts-accessibility"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Zolgensma’s Price And Its &#39;Cure One, Cure Many&#39; Potential &amp; Concerts Accessibility
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1566345600" data-format="short_date">Aug 21, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7346690-40-interview-with-kellie-cusack"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35282102/75x75/c 75w, https://audioboom.com/i/35282102/150x150/c 150w, https://audioboom.com/i/35282102/300x300/c 300w, https://audioboom.com/i/35282102/600x600/c 600w, https://audioboom.com/i/35282102/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #594438; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35282102/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
#40 - Interview With Kellie Cusack
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
29m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1566303700" data-format="short_date">Aug 20, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
29m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7345565-high-levels-of-alpha-cop-proteins-seems-to-ease-sma-severity-in-mouse-models-spinraza-for-2-years"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
High Levels of Alpha-COP Proteins Seems To Ease SMA Severity in Mouse Models &amp; Spinraza For 2 Years
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1566172800" data-format="short_date">Aug 19, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7343852-the-rare-barometer-is-helping-eurordis-shape-eu-rare-disease-policies-sma-community-diversity"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
The &quot;Rare Barometer” Is Helping Eurordis Shape EU Rare Disease Policies &amp; SMA Community Diversity
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1565913600" data-format="short_date">Aug 16, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7341894-zolgensma-for-sma-types-1-2-and-3-more-options-on-the-way-angela-titcombe"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
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</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
11m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1565740800" data-format="short_date">Aug 14, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
11m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7339979-ontario-patients-are-granted-with-wider-access-to-spinraza-current-treatments-brighter-futures"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
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</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1565568000" data-format="short_date">Aug 12, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7337855-family-says-zolgensma-saved-all-of-their-lives-their-gene-therapy-tyler-dukes"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
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Family Says Zolgensma Saved All of Their Lives; Their Gene Therapy &amp; Tyler Dukes
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1565308800" data-format="short_date">Aug 09, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7335720-zolgensma-s-potential-to-change-the-whole-landscape-of-sma-melissa-milinovich-s-story"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Zolgensma&#39;s Potential To Change The Whole Landscape of SMA &amp; Melissa Milinovich&#39;s Story
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1565136000" data-format="short_date">Aug 07, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7334680-39-interview-with-jason-bertsch"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35220081/75x75/c 75w, https://audioboom.com/i/35220081/150x150/c 150w, https://audioboom.com/i/35220081/300x300/c 300w, https://audioboom.com/i/35220081/600x600/c 600w, https://audioboom.com/i/35220081/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #3d373c; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35220081/1400x1400/c" />
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<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
#39 - Interview With Jason Bertsch
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
33m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1565049600" data-format="short_date">Aug 06, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
33m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7333633-european-sma-advocates-question-the-eu-s-willingness-to-reimburse-zolgensma-independence"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
European SMA Advocates Question The EU’s Willingness to Reimburse Zolgensma &amp; Independence
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1564963200" data-format="short_date">Aug 05, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7332117-improved-survival-and-key-motor-milestones-achieved-with-risdiplam-stress-management"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Improved Survival And Key Motor Milestones Achieved With Risdiplam &amp; Stress Management
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
7m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1564704000" data-format="short_date">Aug 02, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
7m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7330043-results-from-phase-2-trial-of-spinraza-in-infants-with-sma-support-efficacy-and-safety-sleeping"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Results From Phase 2 Trial of Spinraza in Infants With SMA Support Efficacy And Safety &amp; Sleeping
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1564531200" data-format="short_date">Jul 31, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7328060-spinraza-is-showing-long-term-benefits-in-all-sma-types-sma-awareness-month"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Spinraza Is Showing Long-Term Benefits In All SMA Types &amp; SMA Awareness Month
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1564358400" data-format="short_date">Jul 29, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7326306-avexis-states-zolgensma-is-showing-strong-efficacy-across-sma-types-coping-with-bad-days"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
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</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1564099200" data-format="short_date">Jul 26, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7324321-spinraza-continues-to-demonstrate-safety-and-improvements-in-sma-patients-tips-for-giving-hugs"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
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</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
12m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1563926400" data-format="short_date">Jul 24, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
12m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/7322360-will-the-national-institute-for-health-and-care-recommend-spinraza-treating-each-day-as-a-blessing"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/35156259/75x75/c 75w, https://audioboom.com/i/35156259/150x150/c 150w, https://audioboom.com/i/35156259/300x300/c 300w, https://audioboom.com/i/35156259/600x600/c 600w, https://audioboom.com/i/35156259/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #474747; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/35156259/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Will The National Institute For Health And Care Recommend Spinraza &amp; Treating Each Day As A Blessing
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1563753600" data-format="short_date">Jul 22, 2019</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
8m
</div>
</div>
</div>
</a></div>

</template></turbo-stream>
  <turbo-stream action="replace" target="turbo_pagination"><template><turbo-frame loading="lazy" id="turbo_pagination" src="/channels/4973736.turbo_stream?list=1&amp;page=11"><div aria-hidden="true" class="card rounded-0 border-0 border-bottom">
<div class="card-body df align-items-center placeholder-glow text-black-50">
<div class="w-100">
<h5>
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<div class="w-100">
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<div class="mla">
<span class="placeholder placeholder-sm" style="width:4ch"></span>
</div>
</div>
</div>
<div aria-hidden="true" class="card rounded-0 border-0 border-bottom">
<div class="card-body df align-items-center placeholder-glow text-black-50">
<div class="w-100">
<h5>
<div class="placeholder col-6"></div>
</h5>
<div class="placeholder placeholder-sm" style="width:15ch"></div>
</div>
<div class="mla">
<span class="placeholder placeholder-sm" style="width:4ch"></span>
</div>
</div>
</div>
<div aria-hidden="true" class="card rounded-0 border-0 border-bottom">
<div class="card-body df align-items-center placeholder-glow text-black-50">
<div class="w-100">
<h5>
<div class="placeholder col-6"></div>
</h5>
<div class="placeholder placeholder-sm" style="width:15ch"></div>
</div>
<div class="mla">
<span class="placeholder placeholder-sm" style="width:4ch"></span>
</div>
</div>
</div>
<div aria-hidden="true" class="card rounded-0 border-0 border-bottom">
<div class="card-body df align-items-center placeholder-glow text-black-50">
<div class="w-100">
<h5>
<div class="placeholder col-6"></div>
</h5>
<div class="placeholder placeholder-sm" style="width:15ch"></div>
</div>
<div class="mla">
<span class="placeholder placeholder-sm" style="width:4ch"></span>
</div>
</div>
</div>
<div class="visually-hidden">
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</div>
</turbo-frame></template></turbo-stream>
