Meredith O'Connor on Her Work Raising Awareness of Myasthenia Gravis
26: Dr. Courtney Young Discusses Her Company’s Approach to Treating DMD
25: Dr. Henry Lin on the Difficulty of Diagnosing LAL-D in Children
24: An Interview With Dr. Albert Faro, vice president for clinical affairs at the Cystic Fibrosis Foundation
23: An Interview With Christine Há, award-winning chef and NMOSD patient
22: Dr. Reham Abdel-Wahab Discusses Cholangiocarcinoma Therapies and Possible Future Advances
21: An Interview With Lisa Phelps Sarfaty of the National Organization for Rare Disorders Ahead of Rare Disease Day
20: An Interview With Evanthia Bernitsas, Director of the Multiple Sclerosis Treatment and Immunology Clinical Research Center at Wayne State University
19: An Interview With Nicola Longo, MD, PhD,professor of pediatrics and chief of the University of Utah's Division of Medical Genetics in Salt Lake City.
18: An Interview With MeiLan K. Han, MD, MS, chief of the University of Michigan’s Division of Pulmonary & Critical Care.
17: An Interview With Sigbjørn Berentsen, MD, PhD, a hematologist and senior researcher at Norway’s Haugesund Hospital.
16: An Interview With Researcher Adrian Krainer, PhD, From the Cold Spring Harbor Laboratory in New York.
15: An interview With Michael Yeaman, PhD, chief medical advisor to the Guthy-Jackson Charitable Fund
14: An Interview With Donald S. Wood, PhD, president and CEO of the Muscular Dystrophy Association
13: Advocating for Patients and Families Affected by Cold Agglutinin Disease
12: Kamada CEO Amir London Discusses the Company's Work on AATD Therapies
11: Endocrine Surgeon Dr. Haggi Mazeh Describes the Challenges of Treating MTC
10: Harsha K. Rajasimha, PhD, on Making Clinical Trials More Inclusive
9: Yale University professor Dr. Naftali Kaminski discusses a new consortium for pulmonary fibrosis with senior correspondent Larry Luxner
8: Durhane Wong-Rieger, PhD, Discusses the Challenges Faced by Rare Disease Patients in Canada
7: A Discussion on Medullary Thyroid Carcinoma With Dr. David Goldenberg
The Pursuit of Redosable Gene Therapies for Hemophilia with Dr. Doug Kerr
Perspectives on Long Chain Fatty Oxidation Disorder With Dr. Jerry Vockley
6: Dr. Hagit Baris-Feldman Discusses Israel's Burgeoning Role in Rare Disease Clinical Research
5: Dr. Noah Greenspan Discusses on the Diagnosis and Treatment of Patients With PAH
Dr. Barry Byrne on Recent Developments in Pompe Disease
4: Dr. Eric Olson Discusses the Use of Gene Therapy in the Treatment of Duchenne Muscular Dystrophy
3: An Interview With Dr. Edward Neilan, Chief Medical Officer at NORD
An Update on LAL-D With Dr. Paul Martin of Nationwide Children's Hospital
Insights From Dr. Noah Greenspan: Diagnosing and Treating IPF
Advocating for People With Gastrointestinal Stromal Tumor
2: Dr. Mark Brantly on Treating AATD and the Work of the Alpha-1 Foundation
1: Ultragenyx CMO Dr. Camille Bedrosian Discusses the First FDA-Approved Treatment for LCFAOD