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<a class="text-decoration-none" href="/posts/8062359-meredith-o-connor-on-her-work-raising-awareness-of-myasthenia-gravis"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Meredith O&#39;Connor on Her Work Raising Awareness of Myasthenia Gravis
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, talks with Meredith O’Connor, a patient advocate and founder of a chronic illness consultancy, about her efforts to raise awareness of myasthenia gravis.
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
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<span><span class="js-time" data-epochtime="1649274851" data-format="short_date">Apr 06, 2022</span></span>
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<hr class="mvn mhs text-black-50 opacity-25">
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<a class="text-decoration-none" href="/posts/8057219-dr-courtney-young-discusses-her-company-s-approach-to-treating-dmd"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
26: Dr. Courtney Young Discusses Her Company’s Approach to Treating DMD
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
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<span><span class="js-time" data-epochtime="1648666442" data-format="short_date">Mar 30, 2022</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
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8m
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<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8053383-dr-henry-lin-on-the-difficulty-of-diagnosing-lal-d-in-children"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
25: Dr. Henry Lin on the Difficulty of Diagnosing LAL-D in Children
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Henry Lin, MD, a pediatric hepatologist with Oregon Science &amp; Health University in Portland. Dr. Lin speaks about the difficulty of diagnosing lysosomal acid lipase deficiency (LAL-D) in children.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
8m
</span>
<span class="d-sm-none">
&bull;
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<span><span class="js-time" data-epochtime="1648061668" data-format="short_date">Mar 23, 2022</span></span>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
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8m
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8053369-an-interview-with-dr-albert-faro-vice-president-for-clinical-affairs-at-the-cystic-fibrosis-fou"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
24: An Interview With Dr. Albert Faro, vice president for clinical affairs at the Cystic Fibrosis Foundation
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
14m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1647964800" data-format="short_date">Mar 22, 2022</span></span>
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</div>
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<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
14m
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8053370-an-interview-with-christine-ha-award-winning-chef-and-nmosd-patient"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
23: An Interview With Christine Há, award-winning chef and NMOSD patient
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Christine Há — a blind chef who not only won Season 3 of the reality TV show &quot;MasterChef&quot; in 2012 but went on to write a bestselling cookbook and later opened two restaurants in Houston, Texas. Há, who has neuromyelitis optica spectrum disorder, is the public face of the new campaign &quot;NMOSD Won&#39;t Stop Me.&quot;
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<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
12m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1647446400" data-format="short_date">Mar 16, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
12m
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</div>
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</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8043131-dr-reham-abdel-wahab-discusses-cholangiocarcinoma-therapies-and-possible-future-advances"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
22: Dr. Reham Abdel-Wahab Discusses Cholangiocarcinoma Therapies and Possible Future Advances
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Reham Abdel-Wahab, MD, PhD, chief scientific officer of the Cholangiocarcinoma Foundation. Dr. Abdel-Wahab discusses recently approved therapies for this rare, aggressive bile duct cancer as well as new advances that may offer hope to patients with the disease.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
12m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1646666796" data-format="short_date">Mar 07, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
12m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8037412-an-interview-with-lisa-phelps-sarfaty-of-the-national-organization-for-rare-disorders-ahead-of-ra"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
21: An Interview With Lisa Phelps Sarfaty of the National Organization for Rare Disorders Ahead of Rare Disease Day 
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Lisa Phelps Sarfaty ahead of February 28, Rare Disease Day. Sarfaty is vice president of community engagement at the National Organization for Rare Disorders (NORD), a coalition of 330 patient advocacy groups and the leading voice for an estimated 25 million Americans with rare and debilitating illnesses.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
10m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1645717443" data-format="short_date">Feb 24, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
10m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8027872-an-interview-with-evanthia-bernitsas-director-of-the-multiple-sclerosis-treatment-and-immunology"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
20: An Interview With Evanthia Bernitsas, Director of the Multiple Sclerosis Treatment and Immunology Clinical Research Center at Wayne State University
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Evanthia Bernitsas, MD, director of the Multiple Sclerosis Treatment and Immunology Clinical Research Center at Wayne State University in Detroit, Michigan. Dr. Bernitsas is an expert on NMOSD and its effect on patients of African origin.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
13m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1644349505" data-format="short_date">Feb 08, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
13m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8023062-an-interview-with-nicola-longo-md-phd-professor-of-pediatrics-and-chief-of-the-university-of-ut"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
19: An Interview With Nicola Longo, MD, PhD,professor of pediatrics and chief of the University of Utah&#39;s Division of Medical Genetics in Salt Lake City. 
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
6m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1643736656" data-format="short_date">Feb 01, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
6m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8016548-an-interview-with-meilan-k-han-md-ms-chief-of-the-university-of-michigan-s-division-of-pulmon"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
18: An Interview With MeiLan K. Han, MD, MS, chief of the University of Michigan’s Division of Pulmonary &amp; Critical Care.
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews MeiLan K. Han, MD, chief of the University of Michigan’s Division of Pulmonary &amp; Critical Care in Ann Arbor. Dr. Han, a spokeswoman for the American Lung Association, leads groundbreaking research on oxygen delivery in chronic lung disease and has also written a book on the subject.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
14m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1642725995" data-format="short_date">Jan 21, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
14m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8012444-an-interview-with-sigbjorn-berentsen-md-phd-a-hematologist-and-senior-researcher-at-norway-s-h"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
17: An Interview With Sigbjørn Berentsen, MD, PhD, a hematologist and senior researcher at Norway’s Haugesund Hospital. 
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Sigbjørn Berentsen, MD, PhD, a hematologist and senior researcher at Norway’s Haugesund Hospital. Dr. Berentsen is an expert in the role of carnitine in regulating LCFAOD.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1642091042" data-format="short_date">Jan 13, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010935-an-interview-with-researcher-adrian-krainer-phd-from-the-cold-spring-harbor-laboratory-in-new-y"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
16: An Interview With Researcher Adrian Krainer, PhD, From the Cold Spring Harbor Laboratory in New York.
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews researcher Adrian Krainer, PhD, from the Cold Spring Harbor Laboratory in New York. Dr. Krainer perfected the RNA splicing technique that led to the development of nusinersen, the first treatment for spinal muscular atrophy.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
14m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1641396358" data-format="short_date">Jan 05, 2022</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
14m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010936-an-interview-with-michael-yeaman-phd-chief-medical-advisor-to-the-guthy-jackson-charitable-fund"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
15: An interview With Michael Yeaman, PhD, chief medical advisor to the Guthy-Jackson Charitable Fund
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Michael Yeaman, PhD, chief medical advisor to the Guthy-Jackson Charitable Fund, based in Los Angeles. Dr. Yeaman speaks about neuromyelitis optica spectrum disorder (NMOSD), a rare autoimmune disease that was once thought to be a form of multiple sclerosis.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1638973728" data-format="short_date">Dec 08, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010937-an-interview-with-donald-s-wood-phd-president-and-ceo-of-the-muscular-dystrophy-association"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
14: An Interview With Donald S. Wood, PhD, president and CEO of the Muscular Dystrophy Association
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Donald S. Wood, PhD, president and CEO of the Muscular Dystrophy Association (MDA). Their conversation focuses on the latest therapies for Duchenne muscular dystrophy, Pompe disease, and spinal muscular atrophy, and on the upcoming 2022 MDA Clinical &amp; Scientific Conference.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
13m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1638221339" data-format="short_date">Nov 29, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
13m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010938-advocating-for-patients-and-families-affected-by-cold-agglutinin-disease"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
13: Advocating for Patients and Families Affected by Cold Agglutinin Disease
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Cori Forster, vice-president of the Cold Agglutinin Disease Foundation (CADF) — a nonprofit organization formed to advocate for patients and families affected by CAD. We also talk about research on new therapies for this extremely rare anemic disorder.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
13m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1637249752" data-format="short_date">Nov 18, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
13m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010939-kamada-ceo-amir-london-discusses-the-company-s-work-on-aatd-therapies"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
12: Kamada CEO Amir London Discusses the Company&#39;s Work on AATD Therapies
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Amir London, CEO of Israel&#39;s Kamada — a major biopharmaceutical company that already has an FDA-approved therapy for alpha-1 antitrypsin deficiency, and is now pursuing an inhaled AAT drug for the same disease.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1636482818" data-format="short_date">Nov 09, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010940-endocrine-surgeon-dr-haggi-mazeh-describes-the-challenges-of-treating-mtc"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
11: Endocrine Surgeon Dr. Haggi Mazeh Describes the Challenges of Treating MTC
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Dr. Haggi Mazeh, an endocrine surgeon at Hebrew University&#39;s Hadassah Medical Center in Jerusalem. Dr. Mazeh, one of Israel&#39;s top experts on thyroid cancer, talks extensively about the challenges of treating medullary thyroid carcinoma.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
12m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1635962265" data-format="short_date">Nov 03, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
12m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010941-harsha-k-rajasimha-phd-on-making-clinical-trials-more-inclusive"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
10: Harsha K. Rajasimha, PhD, on Making Clinical Trials More Inclusive
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Harsha K. Rajasimha, PhD, in Herndon, Virginia. Dr. Rajasimha cofounded the Organization for Rare Diseases India and is now CEO of Jeeva Informatics, which aims to improve the diversity, equity, and inclusion (DE&amp;I) of patients in clinical trials worldwide.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
16m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1635266730" data-format="short_date">Oct 26, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
16m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010942-yale-university-professor-dr-naftali-kaminski-discusses-a-new-consortium-for-pulmonary-fibrosis"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
9: Yale University professor Dr. Naftali Kaminski discusses a new consortium for pulmonary fibrosis with senior correspondent Larry Luxner
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, talks to pulmonologist Naftali Kaminski, MD, professor of medicine and pharmacology and chief of Pulmonary, Critical Care and Sleep Medicine at Yale University School of Medicine in New Haven, Connecticut. Dr. Kaminski discusses the recently announced Three Lakes Consortium for Pulmonary Fibrosis (TLC4PF), a consortium involving the T...
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
12m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1634824220" data-format="short_date">Oct 21, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
12m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010943-durhane-wong-rieger-phd-discusses-the-challenges-faced-by-rare-disease-patients-in-canada"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
8: Durhane Wong-Rieger, PhD, Discusses the Challenges Faced by Rare Disease Patients in Canada
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Durhane Wong-Rieger, PhD, president and CEO of the Canadian Organization for Rare Disorders (CORD) and chair of Rare Diseases International (RDI). Dr. Wong-Rieger talks about the challenges of diagnosing and treating diseases in Canada, as well as advancing access to therapies around the globe.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
15m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1634157776" data-format="short_date">Oct 13, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
15m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010944-a-discussion-on-medullary-thyroid-carcinoma-with-dr-david-goldenberg"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
7: A Discussion on Medullary Thyroid Carcinoma With Dr. David Goldenberg
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews David Goldenberg, MD, FACS, a surgical oncologist, and professor and chair of the department of otolaryngology-head and neck surgery at Penn State College of Medicine in Hershey, Pennsylvania. Dr. Goldenberg has just published the latest edition of his book, Endocrine Surgery of the Head and Neck, a significant portion of w...
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
13m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1633528917" data-format="short_date">Oct 06, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
13m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010945-the-pursuit-of-redosable-gene-therapies-for-hemophilia-with-dr-doug-kerr"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
The Pursuit of Redosable Gene Therapies for Hemophilia with Dr. Doug Kerr
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Doug Kerr, MD, PhD, chief medical officer at Generation Bio in Cambridge, Massachusetts. The company is aggressively pursuing redosable gene therapies for hemophilia and other rare diseases.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
21m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1632516941" data-format="short_date">Sep 24, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
21m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010946-perspectives-on-long-chain-fatty-oxidation-disorder-with-dr-jerry-vockley"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818047/75x75/c 75w, https://audioboom.com/i/38818047/150x150/c 150w, https://audioboom.com/i/38818047/300x300/c 300w, https://audioboom.com/i/38818047/600x600/c 600w, https://audioboom.com/i/38818047/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #e3b7b4; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818047/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Perspectives on Long Chain Fatty Oxidation Disorder With Dr. Jerry Vockley 
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Jerry Vockley, MD, PhD, chief of medical genetics at Pennsylvania&#39;s UPMC Children&#39;s Hospital of Pittsburgh. Dr. Vockley is also the founder of INFORM, the International Network for Fatty Acid Oxidation Research and Management, which will hold its next annual conference virtually Oct. 27-28.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
25m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1632410598" data-format="short_date">Sep 23, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
25m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010947-dr-hagit-baris-feldman-discusses-israel-s-burgeoning-role-in-rare-disease-clinical-research"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
6: Dr. Hagit Baris-Feldman Discusses Israel&#39;s Burgeoning Role in Rare Disease Clinical Research
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Hagit Baris-Feldman, MD, director of the Genetics Institute at Israel&#39;s Tel Aviv Sourasky Medical Center. Dr. Baris-Feldman, who also chairs the Israel Medical Genetics Association and is an associate professor at Tel Aviv University&#39;s Sackler Faculty of Medicine, talks about why Israel has emerged as a global leader in the...
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
13m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1632330232" data-format="short_date">Sep 22, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
13m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010948-dr-noah-greenspan-discusses-on-the-diagnosis-and-treatment-of-patients-with-pah"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
5: Dr. Noah Greenspan Discusses on the Diagnosis and Treatment of Patients With PAH
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Noah Greenspan, DPT, founder of New York City&#39;s Pulmonary Wellness &amp; Rehabilitation Center. Dr. Greenspan, who also runs the nonprofit Pulmonary Wellness Foundation, talks about diagnosing and treating pulmonary arterial hypertension.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
17m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1631886244" data-format="short_date">Sep 17, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
17m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010949-dr-barry-byrne-on-recent-developments-in-pompe-disease"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Dr. Barry Byrne on Recent Developments in Pompe Disease
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Barry Byrne, MD, director of the University of Florida&#39;s Powell Gene Therapy Center in Gainesville. Dr. Byrne has spent years researching potential gene therapies for Pompe disease, comments on the FDA&#39;s recent approval of avalglucosidase alfa-ngpt (Nexviazyme) to treat Pompe.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
14m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1631565763" data-format="short_date">Sep 13, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
14m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010950-dr-eric-olson-discusses-the-use-of-gene-therapy-in-the-treatment-of-duchenne-muscular-dystrophy"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
4: Dr. Eric Olson Discusses the Use of Gene Therapy in the Treatment of Duchenne Muscular Dystrophy
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Eric Olson, PhD, chief scientific advisor at Vertex Pharmaceuticals and founding chair of the molecular biology department at the University of Texas-Southwestern Medical Center. Dr. Olson is an expert on Duchenne muscular dystrophy and CRISPR gene editing technology.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
9m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1631128429" data-format="short_date">Sep 08, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
9m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010951-an-interview-with-dr-edward-neilan-chief-medical-officer-at-nord"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
3: An Interview With Dr. Edward Neilan, Chief Medical Officer at NORD
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Edward Neilan, MD, chief medical officer at the National Organization for Rare Disorders (NORD). This is a new position at NORD, which serves as the umbrella organization for some 330 disease-specific patient advocacy groups. NORD also sponsors the annual Rare Diseases and Orphan Products Breakthrough Summit, which this yea...
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
21m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1631029678" data-format="short_date">Sep 07, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
21m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010952-an-update-on-lal-d-with-dr-paul-martin-of-nationwide-children-s-hospital"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
An Update on LAL-D With Dr. Paul Martin of Nationwide Children&#39;s Hospital 
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
15m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1630530333" data-format="short_date">Sep 01, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
15m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010953-insights-from-dr-noah-greenspan-diagnosing-and-treating-ipf"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818047/75x75/c 75w, https://audioboom.com/i/38818047/150x150/c 150w, https://audioboom.com/i/38818047/300x300/c 300w, https://audioboom.com/i/38818047/600x600/c 600w, https://audioboom.com/i/38818047/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #e3b7b4; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818047/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Insights From Dr. Noah Greenspan: Diagnosing and Treating IPF
</h5>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
23m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1630526687" data-format="short_date">Sep 01, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
23m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010954-advocating-for-people-with-gastrointestinal-stromal-tumor"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818047/75x75/c 75w, https://audioboom.com/i/38818047/150x150/c 150w, https://audioboom.com/i/38818047/300x300/c 300w, https://audioboom.com/i/38818047/600x600/c 600w, https://audioboom.com/i/38818047/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #e3b7b4; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818047/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
Advocating for People With Gastrointestinal Stromal Tumor
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Peter Knox, senior research director at the Life Raft Group. Based in Wayne, New Jersey, this organization was incorporated in 2002 and advocates for people with all forms of gastrointestinal stromal tumor, or GIST.
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
31m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1630425420" data-format="short_date">Aug 31, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
31m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010955-dr-mark-brantly-on-treating-aatd-and-the-work-of-the-alpha-1-foundation"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
2: Dr. Mark Brantly on Treating AATD and the Work of the Alpha-1 Foundation
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Dr. Brantly is the vice-chair of research in the Department of Medicine at the University of Florida in Gainesville, and has spent most of his career researching a cure for alpha-1 antitrypsin deficiency (AATD).
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
12m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1629226811" data-format="short_date">Aug 17, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
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12m
</div>
</div>
</div>
</a></div>
<hr class="mvn mhs text-black-50 opacity-25">
<div class="card rounded-0 border-0 pas qa-audio-clip-overview" style="--bs-card-bg: transparent;">
<a class="text-decoration-none" href="/posts/8010956-ultragenyx-cmo-dr-camille-bedrosian-discusses-the-first-fda-approved-treatment-for-lcfaod"><div class="Episode-list-grid card-body pan">
<div class="l-flex align-items-baseline gap-2 gap-md-3">
<img srcset="https://audioboom.com/i/38818050/75x75/c 75w, https://audioboom.com/i/38818050/150x150/c 150w, https://audioboom.com/i/38818050/300x300/c 300w, https://audioboom.com/i/38818050/600x600/c 600w, https://audioboom.com/i/38818050/1400x1400/c 1400w" sizes="(max-width: 400px) 64px, 96px" style="background-color: #ddb4b1; max-width: 96px; width: 15cqw;" class="js-img-bg ratio-square rounded-1" loading="lazy" src="https://audioboom.com/i/38818050/1400x1400/c" />
<div class="vstack gap-1 my-auto">
<h5 class="text-line-clamp text-line-clamp-3 balanced-h fs-6 fs-5-lg fw-normal mb-0">
1: Ultragenyx CMO Dr. Camille Bedrosian Discusses the First FDA-Approved Treatment for LCFAOD
</h5>
<div class="text-line-clamp text-line-clamp-3 balanced-p fs-8 text-muted text-break">
Larry Luxner, senior correspondent for Rare Disease Advisor, interviews Camille Bedrosian, MD, chief medical officer and executive vice president of Ultragenyx Pharmaceutical in Novato, California. Earlier this year, Ulragenyx won approval from the US Food and Drug Administration (FDA) for triheptanoin (Dojolvi®), a liquid medication that supplies medium-chain, odd-carbon fatty acids as an ener...
</div>
<div class="text-muted df align-items-baseline gap-2 fs-8">
<span class="numeric-tabular d-sm-none">
14m
</span>
<span class="d-sm-none">
&bull;
</span>
<span><span class="js-time" data-epochtime="1628691149" data-format="short_date">Aug 11, 2021</span></span>
</div>
</div>
</div>
<div class="d-none d-sm-grid" style="justify-self: center; align-items: center;">
<div class="fs-8 numeric-tabular text-nowrap text-muted phs">
14m
</div>
</div>
</div>
</a></div>

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