Pharmaceutical Executive Daily: Ultragenyx's Apazunersen Fails Phase III Trial
Sep 03, 05:27 PM
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Ultragenyx shares plunge after apazunersen fails its Phase III trial in Angelman syndrome, Mark Cziraky of Carelon Research talks through the mechanics of analyzing linked real-world data sets, and Melanie Whittington joins The Ron Lanton Report to argue biopharma policy needs to stay tethered to patients, not abstractions.
